Palynziq (pegvaliase), new treatment for phenylketonuria, a rare inherited metabolic disease

EMA’s human medicines committee (CHMP) has recommended the authorisation of…


Zynquista (sotagliflozin), New add-on treatment to insulin for treatment of certain patients with type 1 diabetes

EMA’s human medicines committee (CHMP) has adopted a positive opinion for…


The World Health Organisation issues an alert on falsified ICLUSIG traded globally

The Medical Product Alert relates to confirmed falsified versions of ICLUSIG…


Cablivi (caplacizumab-yhdp) approved by FDA for the treatment of acquired thrombotic thrombocytopenic purpura (aTTP)

The U.S. Food and Drug Administration has approved Cablivi (caplacizumab-yhdp)…


First generic version of Sabril (vigabatrin) approved by FDA for the treatment of complex partial seizures

The U.S. Food and Drug Administration approved the first generic version of…


Ultomiris (ravulizumab), approved by FDA for the treatment of paroxysmal nocturnal hemoglobinuria (PNH)

The U.S. Food and Drug Administration has approved Ultomiris (ravulizumab)…


FDA approves Elzonris (tagraxofusp-erzs), first treatment for rare blood disease

The U.S. Food and Drug Administration has approved Elzonris (tagraxofusp-erzs)…


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